"It is against the basic civil and human rights that we have established are a key part of American identity," one advocate ...

Rollout of YORVIPATH® initiated in Germany and Austria, with an estimated 55 doctors writing prescriptions and ~100 patients ...

People with Laron syndrome have a low risk of heart disease and a number of other age-related disorders, hinting at ...

Amber Johnston, who is a familiar face on the popular reality TV series 7 Little Johnstons, recently shared a heartfelt ...

Presented cardiac magnetic resonance (CMR) imaging evidence consistent with clinical improvement observed in patients with ...

Leerink Partners analyst Mani Foroohar has maintained their bullish stance on BBIO stock, giving a Buy rating on April 30. Mani ...

Actress Samantha’s dad Peter was an extra alongside her in ‘Willow’ and she had achondroplasia – a bone growth disorder that ...

Bexagliflozin (Brenzavvy) and dapagliflozin (Farxiga) induced similar HbA1c reductions over 24 weeks in a head-to-head phase ...

Analyst Paul Choi from Goldman Sachs maintained a Buy rating on BridgeBio Pharma (BBIO – Research Report) and keeping the price target at ...

A TV showrunner can anticipate or plan for any number of things, such as a cast member walking away from a role that he/she ...

After BioMarin’s new leadership conducted a “strategic R&D asset review,” three of its “most productive” assets are being ...

VOXZOGO in achondroplasia continues towards blockbuster status. The majority of new U.S. prescriptions in the quarter were ...