"It is against the basic civil and human rights that we have established are a key part of American identity," one advocate ...

People with Laron syndrome have a low risk of heart disease and a number of other age-related disorders, hinting at ...

Amber Johnston, who is a familiar face on the popular reality TV series 7 Little Johnstons, recently shared a heartfelt ...

an oral FGFR1-3 selective tyrosine kinase inhibitor for the treatment of FGFR-driven cancers and in preclinical development for the treatment of achondroplasia; and BBP-631, a preclinical ...

Rollout of YORVIPATH® initiated in Germany and Austria, with an estimated 55 doctors writing prescriptions and ~100 patients ...

Leerink Partners analyst Mani Foroohar has maintained their bullish stance on BBIO stock, giving a Buy rating on April 30. Mani ...

Presented cardiac magnetic resonance (CMR) imaging evidence consistent with clinical improvement observed in patients with ...

The federal data, published in a report Tuesday, covers 2010 through 2022 and finds rural Americans to be at higher risk of early death from one of the five leading causes of death: heart disease, ...

After BioMarin’s new leadership conducted a “strategic R&D asset review,” three of its “most productive” assets are being ...

Harry Potter and Star Wars actor Warwick Davis' children have shared their heartbreaking tribute to their mum, Samantha, ...

VOXZOGO in achondroplasia continues towards blockbuster status. The majority of new U.S. prescriptions in the quarter were ...