"It is against the basic civil and human rights that we have established are a key part of American identity," one advocate ...

People with Laron syndrome have a low risk of heart disease and a number of other age-related disorders, hinting at ...

Topline data from pivotal ApproaCH Trial expected in the fourth quarter of 2024, and plan to submit a New Drug Application to FDA for children with achondroplasia (age 2-11 years) in the same quarter.

Amber Johnston, who is a familiar face on the popular reality TV series 7 Little Johnstons, recently shared a heartfelt ...

Presented cardiac magnetic resonance (CMR) imaging evidence consistent with clinical improvement observed in patients with ...

Leerink Partners analyst Mani Foroohar has maintained their bullish stance on BBIO stock, giving a Buy rating on April 30. Mani ...

The federal data, published in a report Tuesday, covers 2010 through 2022 and finds rural Americans to be at higher risk of early death from one of the five leading causes of death: heart disease, ...

Warwick Davis has announced the death of his wife, Samantha, aged 53. The Harry Potter actor shared a touching tribute to his ...

After BioMarin’s new leadership conducted a “strategic R&D asset review,” three of its “most productive” assets are being ...

BioMarin Pharmaceutical Inc. (NASDAQ: BMRN) today announced financial results for the quarter ended March 31, 2024.

VOXZOGO in achondroplasia continues towards blockbuster status. The majority of new U.S. prescriptions in the quarter were ...